Current Clinical Trials

Duchenne Muscular Dystrophy

FOR-DMD - Ongoing, Recruitment Complete

Finding the Optimum Regimen for Duchenne Muscular Dystrophy (FOR-DMD)

 

Canadian sites:

1)   Alberta Children's Hospital -Calgary,AB

2)   Children's Hospital- London Health Sciences Centre - London, ON

3)   Children's Hospital of Eastern Ontaio - Ottawa, ON

4)   British Columbia's Children's Hospital- Vancouver, BC

 

 

For more information and participant eligibility  visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/NCT01603407?term=for-DMD&rank=1

Spinal Muscular Atrophy

SMNRx- ISIS - Ongoing, Recruitment complete.

A Study to Assess the Safety, Tolerability, and Pharmacokinetics of Multiple Doses of ISIS 396443 Delivered Intrathecally to Patients With Infantile-Onset Spinal Muscular Atrophy 

 

Canadian sites:

1) Hospital for Sick Children - Toronto, ON

 

For more information and participant eligibility visit the clinical trial site below:

https://clinicaltrials.gov/ct2/show/NCT01839656?term=SMA+ISIS&rank=1

Myoblast Transplantation in Duchenne Muscular Dystrophy - Recruiting

Canadian sites:

1)   Children's Hospital- London Health Sciences Centre - London, ON

2)   Centre de recherche du CHU de Québec - CHUL

For more information and participant eligibility  visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/NCT02196467?cond=dmd&cntry=CA&rank=1

STEADFAST - Funding provided by Jesse's Journey  Ongoing, Recruitment complete

Stacking Exercises Aid the Decline in FVC and Sick Time (STEADFAST)

 

Canadian Sites::

1)    Alberta Children's Hospital- Calgary, AB

2)    Stollery Children's Hospital- Edmonton, AB

3)    BC Children's Hospital - Vancouver, BC

4)    Children's Hospital Health Sciences Centre Winnipeg - Winnipeg, MB

5)    IWK Grace Children's Hospital - Halifax, NS

6)    McMaster University - Hamilton, ON

7)    Children's Hospital- London Health Sciences Centre - London, ON

8)    Children's Hospital of Eastern Ontario - Ottawa, ON

9)    Holland Bloorview Kids Rehabilitation Hospital - Toronto, ON

10)   Erin Oak - Toronto, ON

11)    SickKids Hospital - Toronto, ON

12)   Hôpital Ste. Justine - Montreal, QC

13)   Centre Hospitalier Universitaire de Québec - Québec, QC

 

For more information and participant eligibility visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/NCT01999075?term=steadfast&rank=1

 

 

 

 

Ataluren - PTC Therapeutics - Ongoing, not recruiting

Study of Ataluren for Previously Treated Patients With nmDBMD in Europe, Israel, Australia, and Canada

 

Candian Sites

1)  Alberta Children's Hospital- Calgary, AB

2)  BC Children's Hospital - Vancouver, BC

3)  Children's Hospital- London Health Sciences Centre - London, ON

 

For more information visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/NCT01557400?term=ptc124&rank=12

 

​​Givinostat - Italfarmaco -Recruiting

Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy

Candian Sites

1)  Alberta Children's Hospital- Calgary, AB

For more information visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/study/NCT02851797?cond=dmd&cntry=CA&draw=2&rank=13&show_locs=Y

SRP-4045 and SRP-4053 - Sarepta - Recruiting

A Double-Blind, Placebo-Controlled, Multi-Center Study with an Open-Label Extension to Evaluate the Efficacy and Safety of SRP-4045 and SRP-4053 in Patients with Duchenne Muscular Dystrophy (ESSENCE)

Candian Sites

1)  Alberta Children's Hospital- Calgary, AB

2)  Children's Hospital- London Health Sciences Centre - London, ON

For more information visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/study/NCT02500381?cond=dmd&cntry=CA&draw=3&rank=14&show_locs=Y

 

 

BMS-986089 - Hoffman - La Roche - Recruiting

A Randomized, Double Blind, Placebo-Controlled, Study to Assess the Efficacy, Safety, and Tolerability of BMS-986089 in Ambulatory Boys with Duchenne Muscular Dystrophy

Canadian Sites::

1)    Alberta Children's Hospital- Calgary, AB

2)    Children's Hospital- London Health Sciences Centre - London, ON

3)    Children's Hospital of Eastern Ontario - Ottawa, ON

4)    McMaster University Health Sciences Centre

For more information visit the clinical trials website below:

https://clinicaltrials.gov/ct2/show/study/NCT03039686?cond=DMD&cntry=CA&rank=7&show_locs=Y

Past meetings have been supported by:

 

CONTACT CPNG

Rhiannon.Hicks@lhsc.on.ca

Phone 519-685-8441

Fax 519-685-8350

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